The role of the viral vector in today’s gene therapy advancements.
Scientists in the field of gene therapy can deliver a functioning gene into the retina of the human eye, using viruses as the transporter of that gene. The viral vector is the microscopic powerhouse in these efforts—and something you will want to know about!
We are constantly connecting with folks in the IRD community to bring new stories to aSharedVision. Check out the latest additions.
Tyler Kitchengs and his grandfather were both diagnosed with retinitis pigmentosa as young boys. The difference in their experiences, however, is measured by more than years. Scientific advances in genetic testing and gene therapy research are transforming the diagnostic journey.
Read their story
Growing up with a sister who slowly lost her sight to retinitis pigmentosa (RP) could never have prepared April Lufriu, former Mrs. World, for the diagnosis of her own two children. Then, when the retinal specialist asked to examine Lufriu’s eyes, the world slid sideways. Read her story
Did you know there are as many as 7,000 rare diseases impacting the lives of ~25–30 million Americans, many of them children? To commemorate Rare Disease Day 2018 and raise awareness of these diseases, we encourage patients to share their stories, build communities, and help advance research for change. Read more